Geneva, June 20 -- International Clinical Trials Registry received information related to the study (ISRCTN91900773) titled 'Observational long-term follow- up study for patients previously treated with ex vivo gene therapy' on June 11.
Study Type: Observational
Study Design:
Observational, long -term follow-up post gene therapy (Safety, Efficacy)
Primary Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust
Condition:
Medical condition: X-linked SCID (SCID-X1)
p47 deficient Autosomal Recessive Chronic Granulomatous Disease (AR-CGD) and Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)
Genetic Diseases
Intervention:
Patients will continue to receive routine medical care and follow...