U.S., Aug. 15 -- ClinicalTrials.gov registry received information related to the study (NCT07123155) titled 'Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)' on July 25.
Brief Summary: The purpose of this study is to evaluate the safety, pharmacodynamics (PD), and exploratory clinical efficacy of S-606001 in adult participants with LOPD as an add-on to ERT.
Study Start Date: Oct. 30
Study Type: INTERVENTIONAL
Condition:
Pompe Disease
Intervention:
DRUG: S-606001
S-606001 administered orally
DRUG: Placebo
S-606001 matching placebo administered orally
Recruitment Status: NOT_YET_RECRUITING
Sponsor: Shionogi
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