Tokyo, Oct. 2 -- UMIN Clinical Trials Registry (UMIN-CTR) received information related to the study (UMIN000059255) titled 'Reliability Assessment of Disease-Specific Patient-Reported Outcomes in Gaucher Disease and Their Correlation with Clinical Information' on Oct. 1.
Study Type:
Observational
Primary Sponsor:
Institute - Kansai Medical University
Condition:
Condition - Gaucher disease
Classification by malignancy - Others
Genomic information - NO
Objective:
Narrative objectives1 - We will validate the criterion-related validity and test-retest reliability of patient-reported outcomes (PROs) developed for patients with Gaucher disease, as well as the minimal clinically important distance (MID) in clinical practice.
Basic objectives2...