U.S., June 25 -- ClinicalTrials.gov registry received information related to the study (NCT07035145) titled 'Observational Cohort Study of Dysferlinopathy in China' on June 04.
Brief Summary: The cohort data to be collected aims to evaluate the phenotype, disease progression, natural history, as well as molecular, genetic, and morphological characteristics of dysferlinopathies (LGMD2B/Miyoshi) in China, contributing to the development of clinical outcome measures and the identification of potential biomarkers for future clinical trials.
Study Start Date: May 01, 2024
Study Type: OBSERVATIONAL
Condition:
Dysferlinopathy
Recruitment Status: COMPLETED
Sponsor: Peking University First Hospital
Information provided by (Responsible Party)...