Clinical Trial: Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients with Duchenne Muscular Dystrophy

U.S., March 29 -- ClinicalTrials.gov registry received information related to the study (NCT06900049) titled 'Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients with Duchenne Muscular Dystrophy' on March 23.

Brief Summary: The purpose of this study is to evaluate the safety, tolerability, and efficacy of LE051 intravenous therapy in DMD patients treated with exon 51 skipping therapy.

Study Start Date: Oct. 24, 2024

Study Type: INTERVENTIONAL

Condition: Duchenne Muscular Dystrophy (DMD)

Intervention: DRUG: LE051

LE051 dose escalation : dose 1 and dose 2.

Recruitment Status: RECRUITING

Sponsor: Shanghai Jiao Tong University School of Medicine

Information provided by (Responsible Party): Jiwen Wang, Shanghai J...