U.S., Feb. 28 -- ClinicalTrials.gov registry received information related to the study (NCT06849609) titled 'A Study to Evaluate the Tolerability, Safety and Efficacy of VGN-R13 in Patients With ALS' on Feb. 23.

Brief Summary: The purpose of this trial is to evaluate safety and efficacy of intrathecal delivery of VGN-R13 as a treatment of Amyotrophic Lateral Sclerosis (ALS).

Study Start Date: Feb., 2025

Study Type: INTERVENTIONAL

Condition: Amyotrophic Lateral Sclerosis (ALS)

Intervention: BIOLOGICAL: VGN-R13

An adeno-associated viral vector 9 delivering human GRN and STMN2 gene.

Recruitment Status: NOT_YET_RECRUITING

Sponsor: Hong Chen

Information provided by (Responsible Party): Hong Chen, Tongji Hospital

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