Clinical Trial: A Study of Patients With Fabry Disease (US Specific)

U.S., April 3 -- ClinicalTrials.gov registry received information related to the study (NCT06906367) titled 'A Study of Patients With Fabry Disease (US Specific)' on March 26.

Brief Summary: This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.

Study Start Date: May, 2025

Study Type: OBSERVATIONAL

Condition: Fabry Disease

Intervention: DRUG: migalastat HCl

Non-interventional study of participants receiving migalastat HCl 150 mg

DRUG: ERT

Non-interventional study of participants receiving enzyme replacement therapy

Recruitment Status: NOT_YET_RECRUITING

Sponsor: Amicus Thera...