U.S., Feb. 21 -- ClinicalTrials.gov registry received information related to the study (NCT07423026) titled 'A Remote Study Using Technology to Assess Outcomes in DMD' on Jan. 05.
Brief Summary: Every year, 100 boys are born in the UK with a rare muscle disease called Duchenne muscular dystrophy. These boys cannot make an important muscle protein called dystrophin. They become weaker as they get older and lose the ability to walk as teenagers. This is a life-limiting condition. There is no cure, but medicines are being made that could help these boys make dystrophin. These medicines are most likely to work best in toddlers, before their muscles become damaged.
There is no way of testing these medicines in children under four. In older chi...