U.S., April 12 -- ClinicalTrials.gov registry received information related to the study (NCT06924125) titled 'Spanish Natural History Study for LAMA2 Muscular Dystrophy' on March 07.
Brief Summary: The objective of this natural history study is to comprehensively characterize the disease progression and clinical features of LAMA2-related dystrophies (LAMA2-RD) in the pediatric population. The study aims to establish a well-defined cohort of patients in Spain, enabling long-term follow-up and facilitating recruitment for future clinical trials.
Study Start Date: July 27, 2021
Study Type: OBSERVATIONAL
Condition:
LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)
Merosin Deficient CMD (Full or Partial)
Merosin Deficient Co...