U.S., Feb. 4 -- ClinicalTrials.gov registry received information related to the study (NCT06805695) titled 'Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)' on Dec. 20, 2024.
Brief Summary: This LTFU is being conducted to assess long-term safety and durability of response in participants dosed with IP in a parent protocol, and to collect longitudinal natural history in enrolled but not dosed participants who also participated in a parent protocol.
Study Start Date: Dec. 23, 2024
Study Type: OBSERVATIONAL
Condition:
Ornithine Transcarbamylase Deficiency
Ornithine Transcarbamylase Deficiency Disease
Urea Cycle Disorders, Inborn
Intervention:
OTHER: No Intervention
No Interv...