U.S., May 3 -- ClinicalTrials.gov registry received information related to the study (NCT06955897) titled 'Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA' on April 25.
Brief Summary: The purpose of this project is to investigate the utility of the SMA EFFORT, an SMA-specific patient-reported outcome measure, to assess perceived physical fatigability that is anchored to intensity and duration of activities. We aim to characterize perceived physical fatigability (PPF) in a diverse cohort of people with SMA (pwSMA) and evaluate the change of PPF before and after nusinersen dosing.
Study Start Date: April 24
Study Type: OBSERVATIONAL
Condition:
Spinal Muscular Atrophy
Intervention:
OTHER: Observational
Observat...