Clinical Trial: A Study to Evaluate the Effects and Safety of Hydroxocobalamin in Participants With Combined Methylmalonic Academia (cblC Type)

U.S., Sept. 10 -- ClinicalTrials.gov registry received information related to the study (NCT07163364) titled 'A Study to Evaluate the Effects and Safety of Hydroxocobalamin in Participants With Combined Methylmalonic Academia (cblC Type)' on Aug. 19.

Brief Summary: This study is a Single-Center, Single-Arm, open-label, Phase III clinical study to evaluate the efficacy, safety characteristics of Hydroxocobalamin Chloride Injection (20 mg/mL) for Maintenance Therapy in participants with Methylmalonic Acidemia (MMA) with Elevated Homocysteine (Cobalamin C Deficiency).

Study Start Date: Aug. 31

Study Type: INTERVENTIONAL

Condition: Methylmalonic Acidemia (MMA)

Intervention: DRUG: Hydroxocobalamin Chloride Injection

1 - 20 mg per dose, 1...