U.S., May 2 -- ClinicalTrials.gov registry received information related to the study (NCT06952686) titled 'A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult Participants' on April 23.
Brief Summary: This is a study of a single systemic dose of SRP-9005 in pediatric and adult participants with limb girdle muscular dystrophy type 2C/R5 (LGMD2C/R5). It is comprised of 2 parts (Part A, Part B) that will assess safety and efficacy.
Study Start Date: May 01
Study Type: INTERVENTIONAL
Condition:
Muscular Dystrophies, Limb-Girdle
Intervention:
BIOLOGICAL: SRP-9005
Solution for single IV infusion
DRUG: Corticosteroid
Oral tablet (prophylactic)
Recruitment Status: NOT_YET_RECRUITING
Sponsor: Sarepta Ther...