Clinical Trial: A Study of Dosing Patterns and Costs in Patients With Spinal Muscular Atrophy Receiving Disease Modifying Therapies

U.S., Jan. 31 -- ClinicalTrials.gov registry received information related to the study (NCT07378943) titled 'A Study of Dosing Patterns and Costs in Patients With Spinal Muscular Atrophy Receiving Disease Modifying Therapies' on Jan. 23.

Brief Summary: The aim of this study was to assess real-world dosing patterns, long-term healthcare costs, and characteristics of SMA patients who received treatment with DMTs. DMTs included onasemnogene abeparvovec, nusinersen, and risdiplam. This study was conducted using both open and closed claims data from the Komodo Health Research Database (KRD+) between 01 January 2016 and 31 October 2024.

Study Start Date: Nov. 06, 2024

Study Type: OBSERVATIONAL

Condition: Muscular Atrophy, Spinal

Recruitment...