Clinical Trial: A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

U.S., Dec. 17 -- ClinicalTrials.gov registry received information related to the study (NCT07285460) titled 'A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B' on Dec. 09.

Brief Summary: This is a parallel, Phase 3, two-arm, open-label study to evaluate the efficacy and safety of treatment with fitusiran prophylaxis administered to male pediatric participants (aged 1 to <12 years) who have severe hemophilia A or B, with or without inhibitory antibodies to FVIII or FIX.

Number of participants:

Approximately 85 participants will be enrolled into the study:

* Approximately 60 fitusiran-naive participants with severe hemophilia A or B, with or wit...