Clinical Trial: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

U.S., Jan. 22 -- ClinicalTrials.gov registry received information related to the study (NCT07354724) titled 'A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease' on Jan. 12.

Brief Summary: This is a Phase 1, multicenter, open-label study to evaluate the safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of DNL952 in adult participants with late-onset Pompe disease. The principal aim of this study is to obtain safety and tolerability data across varous dose levels of DNL952 in participants with late-onset Pompe disease (LOPD).

Study Start Date: March, 2026

Study Type: INTERVENTIONAL

Condition: Late-onset Pompe Disease

Intervention: DRU...