Clinical Trial: A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Participants With Duchenne Muscular Dystrophy (DMD)

U.S., Oct. 28 -- ClinicalTrials.gov registry received information related to the study (NCT05096221) titled 'A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Participants With Duchenne Muscular Dystrophy (DMD)' on Oct. 14.

Brief Summary: The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The participants who are randomized to the placebo arm will have an opportunity for treatment with gene transfer therapy at the beginning of the second year.

Study Type: Interventional

Condition: Duchenne Muscular Dystrophy

Intervention: * Genetic: SRP-9001

Single IV infusion of SRP-9001.

* Genetic: Placebo

Single IV inf...