U.S., July 11 -- ClinicalTrials.gov registry received information related to the study (NCT07058662) titled 'A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.' on July 01.
Brief Summary: The purpose of the study is to evaluate the safety, tolerability, and efficacy of BBM-D101 to treat participants with Duchenne Muscular Dystrophy.
Study Start Date: June 30
Study Type: INTERVENTIONAL
Condition:
DMD
Intervention:
GENETIC: Single dose intravenous of BBM-D101
BBM-D101 is a gene addition therapy based on engineered AAV delivery therapeutic protein gene cassette into muscle for treating DMD. Therapeutic protein could mediate the dystrophin-associated protein c...